Safety and Efficacy of Ponatinib for Treatment of Pediatric Recurrent or Refractory Leukemias, Lymphomas or Solid Tumors
This is not medical advice. AI-assisted translation — inaccuracies may occur. Always verify the original and consult your oncologist before taking any steps.
About the trial
The purpose of this study is to evaluate the safety, tolerability, pharmacokinetics, and efficacy of ponatinib in children aged 1 to \< 18 years with advanced leukemias, lymphomas, and solid tumors.
Original English text from ClinicalTrials.gov
Who can (and can't) join
✓ Qualifies
- •Potwierdzona diagnoza białaczki (CML, ALL, AML), chłoniaka lub guza litego
- •Wiek od 1 roku do poniżej 18 lat
- •Rak, który nie reaguje na wcześniejsze leczenie lub standard nie jest dostępny
- •W przypadku białaczki CML: oporność na co najmniej jeden poprzedni lek lub mutacja T315I
- •Wynik badania szpiku kostnego potwierdzający rodzaj raka (wykonany w ciągu 42 dni przed rozpoczęciem leczenia)
- •Guz można zmierzyć za pomocą badań obrazowych (CT lub MRI)
Simplified criteria — AI translation
Trial details
- Minimum age
- 1 Year
- Maximum age
- 17 Years
- Last updated (source)
- July 23, 2026
- Sex
- No restrictions
Therapies / drugs in trial
Locations (23)
Ghent University Hospital
Ghent, Belgium
Hopital Robert Debre
Paris, France
Armand Trousseau Hospital
Paris, France
Centre Hospitalier Universitaire de Poitiers
Poitiers, France
Chu de Rennes - Hospital Sud
Rennes, France
Aou Policlinico S. Orsola-Malpighi
Bologna, Italy
Asst Degli Spedali Civili Di Brescia
Brescia, Italy
Ospedale Pediatrico G. Gaslini
Genova, Italy
Comitato Etico Fondazione Irccs Istituto Nazionale Dei Tumori Milano
Milan, Italy
University of Milano Bicocca
Monza, Italy
Aorn Santobono Pausilipon
Naples, Italy
Comitato Di Bioetica Della Fondazione Irccs Policlinico San Matteo
Pavia, Italy
Ospedale Pediatrico Bambino Gesu Irccs
Rome, Italy
A.O.U Citta Della Salute E Della Scienza Di Torino Presidio Ospedaliero Infantile Regina Margherita
Torino, Italy
Princess Maxima Center For Pediatric Oncology
Utrecht, Netherlands
Hospital General Universitario Vall D Hebron
Barcelona, Spain
Hospital Sant Joan de Deu de Manresa
Barcelona, Spain
Hospital Infantil Unversitario Nino Jesus
Madrid, Spain
Hospital Universitari I Politecnic La Fe
Valencia, Spain
Karolinska University Hospital Solna
Stockholm, Sweden
Royal Hospital For Sick Children Yorkhill Glasgow
Glasgow, United Kingdom
Alder Hey Childrens Nhs Foundation Trust
Liverpool, United Kingdom
The Royal Marsden Nhs Foundation Trust - Sutton
Sutton, United Kingdom
Trial contact
Incyte Corporation Call Center (ex-US)
Contact information from ClinicalTrials.gov. Contact in English.
Share this trial
Data from ClinicalTrials.gov. AI-assisted translation, last sync: 7/9/2026.
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