RecruitingPhase IEN originalLeukemia

A Study to Find the Highest Dose of Cedazuridine and Decitabine Combination With Filgrastim as a Treatment Option After Hematopoietic Stem Cell Transplant in Children With High-Risk Acute Myeloid Leukemia

⚠️

This is not medical advice. AI-assisted translation — inaccuracies may occur. Always verify the original and consult your oncologist before taking any steps.

About the trial

This phase I trial tests the safety, side effects, and best dose of ASTX727 and filgrastim for the treatment of children with high risk acute myeloid leukemia that has come back after a period of improvement (recurrent) or that does not respond to treatment (refractory) who have undergone allogenic hematopoietic stem cell transplantation. ASTX727 is a combination of cedazuridine and decitabine. Cedazuridine is in a class of medications called cytidine deaminase inhibitors. It prevents the breakdown of decitabine, making it more available in the body so that decitabine will have a greater effect. Decitabine is in a class of medications called hypomethylation agents. It works by helping the bone marrow produce normal blood cells and by killing abnormal cells in the bone marrow. Filgrastim stimulates the production of neutrophils (a type of white blood cell) which can help to prevent infection. Giving ATSX727 and filgrastim may be safe and tolerable in treating children with high risk, recurrent or refractory acute myeloid leukemia who have undergone allogenic hematopoietic stem cell transplantation.

Original English text from ClinicalTrials.gov

Who can (and can't) join

✓ Qualifies

  • Dzieci do 21. roku życia.
  • Dzieci z ostrym szpiczakiem szpiku, który powrócił po leczeniu lub nie reaguje na leczenie, u których przeprowadzono przeszczep komórek macierzystych.
  • Dzieci, u których choroba jest w fazie remisji przed przeszczepem.
  • Dzieci, które planują pobranie próbki szpiku kostnego do badania przed przeszczepem.

Simplified criteria — AI translation

Trial details

Maximum age
21 Years
Last updated (source)
July 7, 2026
Sex
No restrictions

Therapies / drugs in trial

Locations (8)

Children's Hospital of Alabama

Birmingham, United States

Riley Hospital for Children

Indianapolis, United States

C S Mott Children's Hospital

Ann Arbor, United States

University of Minnesota/Masonic Cancer Center

Minneapolis, United States

Memorial Sloan Kettering Cancer Center

New York, United States

Children's Hospital of Philadelphia

Philadelphia, United States

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, United States

Saint Jude Children's Research Hospital

Memphis, United States

Trial contact

Girish Dhall

PRINCIPAL_INVESTIGATOR

Site Public Contact

Brian D. Weiss

PRINCIPAL_INVESTIGATOR

Site Public Contact

Rajen Mody

PRINCIPAL_INVESTIGATOR

Site Public Contact

Robin L. Williams

PRINCIPAL_INVESTIGATOR

Site Public Contact

Maria Luisa Sulis

PRINCIPAL_INVESTIGATOR

Sarah K. Tasian

PRINCIPAL_INVESTIGATOR

Archana Ramgopal

PRINCIPAL_INVESTIGATOR

Jessica Gartrell

PRINCIPAL_INVESTIGATOR

Contact information from ClinicalTrials.gov. Contact in English.

Share this trial

Data from ClinicalTrials.gov. AI-assisted translation, last sync: 7/8/2026.

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